About Us
Gene therapy offers hope for nearly every field of medicine. In the not-too-distant future, diabetes could be prevented before it occurs. Cancers could be controlled or even cured. Alzheimer's and Parkinson's disease could be cured or significantly delayed. A fetus with Tay-Sachs disease could be genetically treated in the womb. The risk of organ transplant rejection could be dramatically reduced. The Gene Therapeutics Research Institute's researchers, in collaboration with clinical researchers, are seeking medical advances in a wide range of clinical disorders, including:
- Parkinson's and Alzheimer's disease
- Cancers, including brain tumors and breast cancer
- Heart disease
- Organ transplantation
- Metabolic disorders
- Intrauterine fetal disorders
- Diabetes
- Blood diseases
- Inflammatory bowel disease
- Infectious diseases
